index - Thérapie génique pour la DMD & physiopathologie du muscle squelettique

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Cells Dystrophie musculaire de Becker NAD+ Drp1 Invivo Liver Centronuclear myopathy Humans LncRNA Mitochondrial fission Mdx mouse L-Type Allele‐specific silencing therapy Cell Line Male Long noncoding RNA Multi exon skipping Clinical trials Morphogenesis Hear Dystrophy Ex-vivo Molecular docking Myogenesis Skeletal muscle Muscular Dystrophy NNOS Inhibitors Human Umbilical Vein Endothelial Cells Epigenetics Base Sequence Long QT Dystrophin central domain Cachexia Animal/physiopathology Activin Receptors Genomic Duchenne muscular dystrophy Muscle Strength Modificateurs de gènes Myotendinous junction Knockout LKB1 Exon skipping CaV subunits Inbred mdx Dystrophine Dynamin 2 Molecular Sequence Data LncARN Dystrophin-EGFP CTNNB1 Muscle Metabolism Becker muscular dystrophy Gene modifiers Hepatocellular carcinoma Muscle Biology Autophagy Inbred C57BL Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS Calcium Muscle development Muscular Atrophy Dystrophie Musculaire de Duchenne DMD Calcium Channels Delivery CD38 Duchenne DMD dystrophy Antisense oligonucleotides Mice Cultured Becker BMD muscular dystrophy Immunoglobulin Fc Fragments/pharmacology Cardiomyopathie DMO Gene Expression Regulation/drug effects Multi resolution modeling Muscles/physiopathology Homeostasis Gene expression Cell Biology MiARN Animals DMD Muscular dystrophy MES Dystrophin BMD CaVβs Diseases Energy Metabolism/drug effects Génomique Cell homeostasis Duchenne muscular dystrophy DMD Multiresolution modeling Cardiomyopathy Becker muscular dystrophy BMD DHPR α1S Dystrophie Musculaire de Becker BMD